Sponsored Research
Your generosity at work
As a foundation, we are incredibly blessed to have a wonderful community of support embracing our mission and cause. With each and every thoughtful donation, your dollars are put to work funding a variety of important projects. Ranging from therapies for a cure to improving quality of daily life, our goal is to diversify and attack the problem from multiple angles, while being guided by the brightest scientific minds in the rare disease space.
Below you will find a list of currently funded projects and a brief description of each. Thank you for your support.
Identifying Potential Molecular Therapies for the Treatment of CLN3
Weimer Lab, Sanford Research
Antisense Oligonucleotides for the Treatment of CLN3
Dr. Michelle Hastings, Rosalind Franklin University
Characterizing the Molecular Function of CLN3 to Identify Novel Therapeutic Targets
Dr. Stephane Lefrancois, Centre Armand-Frappier Sante Biotechnologie
Defining Peripheral and Enteric Nervous Disease in Juvenile Batten Disease
Dr. Jonathan Cooper, Washington U. School of Medicine
Characterizing Sleep Dysfunction in Individuals with NCL Disorders
Dr. Heather Adams, University of Rochester Medical Center
in Collaboration with the BDSRA
Gene Therapy for Children with Pre-Existing AAV Antibodies
Dr. Kathrin Meyer, Nationwide Children’s Hospital
Dr. Jill Weimer addresses attendees at Take a Swing Fore Batten III
